All Articles tagged antisense oligonucleotide

• Reviews
  June 18, 2021 EDT
  The Antisense Oligonucleotide Nusinersen for Treatment of Spinal Muscular Atrophy
  Amber N. EdinoffLong H. NguyenAmira S. OdishoBenjamin S. MaxeyJohn W. PruittBrook GirmaElyse M. CornettAdam M. KayeAlan D. Kaye

  Nusinersen is a novel therapeutic approach with consistent results in all three studies and is proof of the novel concept for treating SMA and other neurodegenerative disorders in the future.

  Abstract